Support Gene Therapy for CTNNB1 Kids

Fundraiser for Gene Therapy for CTNNB1 Syndrome Children

Help Us Give These Children a Brighter Future

Dear Friends,

We are Akhilesh and Deepti Agarwal, and we have started the CTNNB1 Gene Therapy Foundation in Texas to support gene therapy trials for children with CTNNB1 syndrome, inspired by our son, Aahren Persha.

Our son Aahren, like many other children, is living with CTNNB1 syndrome—a condition that affects his ability to do everyday things like sitting, standing, and speaking. CTNNB1 syndrome is a tough battle for these kids, bringing motor delays, learning difficulties, autism, and cerebral palsy. Every day is a challenge, and it breaks our hearts to see our son and others like him struggle.

But there is hope. The CTNNB1 Foundation (https://ctnnb1-foundation.org/) is leading the charge in finding a cure. The gene therapy trial is set to begin in 2025 in Europe. A clinical examination was conducted on June 15th, 2024, for 83 children, paving the way for this life-changing trial. However, we need your help. To support this trial, we need to raise 1.3 million euros. The money we raise will go to the CTNNB1 Foundation to create doses for gene therapy. The good news is that pre-clinical studies have been incredibly successful, so we know this therapy can make a significant difference.

Please, donate whatever you can. Your contribution could be the difference between a life of struggle and a life full of possibilities for these children.

Thank you for your kindness and support.

CTNNB1 Gene Therapy Foundation is a registered 501(c)(3) nonprofit organization. EIN 99-3901640

With love,

Akhilesh and Deepti